A homozygous MED11 C-terminal variant causes a lethal neurodegenerative disease.
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Calì E, et al.
Genet Med. 2022 Oct;24(10):2194-2203. doi: 10.1016/j.gim.2022.07.013. Epub 2022 Aug 24.
Genet Med. 2022.
PMID: 36001086
Free PMC article.