Base-editing corrects metabolic abnormalities in a humanized mouse model for glycogen storage disease type-Ia.
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Arnaoutova I, et al. Among authors: quinn jj.
Nat Commun. 2024 Nov 10;15(1):9729. doi: 10.1038/s41467-024-54108-1.
Nat Commun. 2024.
PMID: 39523369
Free PMC article.