Creation of de novo cryptic splicing for ALS and FTD precision medicine.
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Wilkins OG, et al. Among authors: barattucci s.
Science. 2024 Oct 4;386(6717):61-69. doi: 10.1126/science.adk2539. Epub 2024 Oct 3.
Science. 2024.
PMID: 39361759
Free PMC article.