Cell-mediated exon skipping normalizes dystrophin expression and muscle function in a new mouse model of Duchenne Muscular Dystrophy.
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Galli F, et al. Among authors: bano otalora b.
EMBO Mol Med. 2024 Apr;16(4):927-944. doi: 10.1038/s44321-024-00031-3. Epub 2024 Mar 4.
EMBO Mol Med. 2024.
PMID: 38438561
Free PMC article.