Gray SJ - Search Results

1

Intrathecal Gene Therapy for Giant Axonal Neuropathy.

Bharucha-Goebel DX, Todd JJ, Saade D, Norato G, Jain M, Lehky T, Bailey RM, Chichester JA, Calcedo R, Armao D, Foley AR, Mohassel P, Tesfaye E, Carlin BP, Seremula B, Waite M, Zein WM, Huryn LA, Crawford TO, Sumner CJ, Hoke A, Heiss JD, Charnas L, Hooper JE, Bouldin TW, Kang EM, Rybin D, Gray SJ, Bönnemann CG; GAN Trial Team. Bharucha-Goebel DX, et al. Among authors: gray sj. N Engl J Med. 2024 Mar 21;390(12):1092-1104. doi: 10.1056/NEJMoa2307952. N Engl J Med. 2024. PMID: 38507752

2

Optimizing gene delivery vectors for the treatment of heart disease.

Gray SJ, Samulski RJ. Gray SJ, et al. Expert Opin Biol Ther. 2008 Jul;8(7):911-22. doi: 10.1517/14712598.8.7.911. Expert Opin Biol Ther. 2008. PMID: 18549322 Review.

3

Reducing the risk of adeno-associated virus (AAV) vector mobilization with AAV type 5 vectors.

Hewitt FC, Li C, Gray SJ, Cockrell S, Washburn M, Samulski RJ. Hewitt FC, et al. Among authors: gray sj. J Virol. 2009 Apr;83(8):3919-29. doi: 10.1128/JVI.02466-08. Epub 2009 Feb 11. J Virol. 2009. PMID: 19211760 Free PMC article.

4

Directed evolution of a novel adeno-associated virus (AAV) vector that crosses the seizure-compromised blood-brain barrier (BBB).

Gray SJ, Blake BL, Criswell HE, Nicolson SC, Samulski RJ, McCown TJ, Li W. Gray SJ, et al. Mol Ther. 2010 Mar;18(3):570-8. doi: 10.1038/mt.2009.292. Epub 2009 Dec 29. Mol Ther. 2010. PMID: 20040913 Free PMC article.

5

Dystrophin immunity in Duchenne's muscular dystrophy.

Mendell JR, Campbell K, Rodino-Klapac L, Sahenk Z, Shilling C, Lewis S, Bowles D, Gray S, Li C, Galloway G, Malik V, Coley B, Clark KR, Li J, Xiao X, Samulski J, McPhee SW, Samulski RJ, Walker CM. Mendell JR, et al. N Engl J Med. 2010 Oct 7;363(15):1429-37. doi: 10.1056/NEJMoa1000228. N Engl J Med. 2010. PMID: 20925545 Free PMC article. Clinical Trial.

6

Optimizing promoters for recombinant adeno-associated virus-mediated gene expression in the peripheral and central nervous system using self-complementary vectors.

Gray SJ, Foti SB, Schwartz JW, Bachaboina L, Taylor-Blake B, Coleman J, Ehlers MD, Zylka MJ, McCown TJ, Samulski RJ. Gray SJ, et al. Hum Gene Ther. 2011 Sep;22(9):1143-53. doi: 10.1089/hum.2010.245. Epub 2011 Jun 1. Hum Gene Ther. 2011. PMID: 21476867 Free PMC article.

7

Preclinical differences of intravascular AAV9 delivery to neurons and glia: a comparative study of adult mice and nonhuman primates.

Gray SJ, Matagne V, Bachaboina L, Yadav S, Ojeda SR, Samulski RJ. Gray SJ, et al. Mol Ther. 2011 Jun;19(6):1058-69. doi: 10.1038/mt.2011.72. Epub 2011 Apr 12. Mol Ther. 2011. PMID: 21487395 Free PMC article.

8

Combination therapy utilizing shRNA knockdown and an optimized resistant transgene for rescue of diseases caused by misfolded proteins.

Li C, Xiao P, Gray SJ, Weinberg MS, Samulski RJ. Li C, et al. Among authors: gray sj. Proc Natl Acad Sci U S A. 2011 Aug 23;108(34):14258-63. doi: 10.1073/pnas.1109522108. Epub 2011 Aug 15. Proc Natl Acad Sci U S A. 2011. PMID: 21844342 Free PMC article.

9

Production of recombinant adeno-associated viral vectors and use in in vitro and in vivo administration.

Gray SJ, Choi VW, Asokan A, Haberman RA, McCown TJ, Samulski RJ. Gray SJ, et al. Curr Protoc Neurosci. 2011 Oct;Chapter 4:Unit 4.17. doi: 10.1002/0471142301.ns0417s57. Curr Protoc Neurosci. 2011. PMID: 21971848 Free PMC article.

10

Viral vectors for gene delivery to the central nervous system.

Lentz TB, Gray SJ, Samulski RJ. Lentz TB, et al. Among authors: gray sj. Neurobiol Dis. 2012 Nov;48(2):179-88. doi: 10.1016/j.nbd.2011.09.014. Epub 2011 Oct 7. Neurobiol Dis. 2012. PMID: 22001604 Free PMC article. Review.

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