High-content screening identifies a small molecule that restores AP-4-dependent protein trafficking in neuronal models of AP-4-associated hereditary spastic paraplegia.
Saffari A, Brechmann B, Böger C, Saber WA, Jumo H, Whye D, Wood D, Wahlster L, Alecu JE, Ziegler M, Scheffold M, Winden K, Hubbs J, Buttermore ED, Barrett L, Borner GHH, Davies AK, Ebrahimi-Fakhari D, Sahin M.
Saffari A, et al. Among authors: barrett l.
Nat Commun. 2024 Jan 17;15(1):584. doi: 10.1038/s41467-023-44264-1.
Nat Commun. 2024.
PMID: 38233389
Free PMC article.