Targeted treatment of severe vascular malformations harboring PIK3CA and TEK mutations with alpelisib is highly effective with limited toxicity.
Sterba M, Pokorna P, Faberova R, Pinkova B, Skotakova J, Seehofnerova A, Blatny J, Janigova L, Koskova O, Palova H, Mahdal M, Pazourek L, Jabandziev P, Slaby O, Mudry P, Sterba J.
Sterba M, et al. Among authors: pazourek l.
Sci Rep. 2023 Jun 28;13(1):10499. doi: 10.1038/s41598-023-37468-4.
Sci Rep. 2023.
PMID: 37380669
Free PMC article.