In vivo HSC prime editing rescues sickle cell disease in a mouse model.
Li C, Georgakopoulou A, Newby GA, Chen PJ, Everette KA, Paschoudi K, Vlachaki E, Gil S, Anderson AK, Koob T, Huang L, Wang H, Kiem HP, Liu DR, Yannaki E, Lieber A.
Li C, et al. Among authors: wang h.
Blood. 2023 Apr 27;141(17):2085-2099. doi: 10.1182/blood.2022018252.
Blood. 2023.
PMID: 36800642
Free PMC article.