Interim safety and efficacy of gene therapy for RLBP1-associated retinal dystrophy: a phase 1/2 trial.
Kvanta A, Rangaswamy N, Holopigian K, Watters C, Jennings N, Liew MSH, Bigelow C, Grosskreutz C, Burstedt M, Venkataraman A, Westman S, Geirsdottir A, Stasi K, André H.
Kvanta A, et al. Among authors: liew msh.
Nat Commun. 2024 Sep 10;15(1):7438. doi: 10.1038/s41467-024-51575-4.
Nat Commun. 2024.
PMID: 39256350
Free PMC article.
Clinical Trial.