Development of a small molecule that corrects misfolding and increases secretion of Z α1 -antitrypsin.
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EMBO Mol Med. 2021 Mar 5;13(3):e13167. doi: 10.15252/emmm.202013167. Epub 2021 Jan 29.
EMBO Mol Med. 2021.
PMID: 33512066
Free PMC article.