Minimal Essential Human Factor VIII Alterations Enhance Secretion and Gene Therapy Efficiency.
Cao W, Dong B, Horling F, Firrman JA, Lengler J, Klugmann M, de la Rosa M, Wu W, Wang Q, Wei H, Moore AR, Roberts SA, Booth CJ, Hoellriegl W, Li D, Konkle B, Miao C, Reipert BM, Scheiflinger F, Rottensteiner H, Xiao W.
Cao W, et al. Among authors: miao c.
Mol Ther Methods Clin Dev. 2020 Oct 22;19:486-495. doi: 10.1016/j.omtm.2020.10.013. eCollection 2020 Dec 11.
Mol Ther Methods Clin Dev. 2020.
PMID: 33313336
Free PMC article.