Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTT.
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Mol Ther Nucleic Acids. 2024 Jun 11;35(3):102246. doi: 10.1016/j.omtn.2024.102246. eCollection 2024 Sep 10.
Mol Ther Nucleic Acids. 2024.
PMID: 39027419
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