AAV CRISPR editing rescues cardiac and muscle function for 18 months in dystrophic mice.
Hakim CH, Wasala NB, Nelson CE, Wasala LP, Yue Y, Louderman JA, Lessa TB, Dai A, Zhang K, Jenkins GJ, Nance ME, Pan X, Kodippili K, Yang NN, Chen SJ, Gersbach CA, Duan D.
Hakim CH, et al. Among authors: kodippili k.
JCI Insight. 2018 Dec 6;3(23):e124297. doi: 10.1172/jci.insight.124297.
JCI Insight. 2018.
PMID: 30518686
Free PMC article.