Antisense oligonucleotide therapy for KCNT1 encephalopathy.
Burbano LE, Li M, Jancovski N, Jafar-Nejad P, Richards K, Sedo A, Soriano A, Rollo B, Jia L, Gazina EV, Piltz S, Adikusuma F, Thomas PQ, Kopsidas H, Rigo F, Reid CA, Maljevic S, Petrou S.
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JCI Insight. 2022 Dec 8;7(23):e146090. doi: 10.1172/jci.insight.146090.
JCI Insight. 2022.
PMID: 36173683
Free PMC article.