Randomized trial of bilateral gene therapy injection for m.11778G>A MT-ND4 Leber optic neuropathy.
Newman NJ, Yu-Wai-Man P, Subramanian PS, Moster ML, Wang AG, Donahue SP, Leroy BP, Carelli V, Biousse V, Vignal-Clermont C, Sergott RC, Sadun AA, Rebolleda Fernández G, Chwalisz BK, Banik R, Bazin F, Roux M, Cox ED, Taiel M, Sahel JA; LHON REFLECT Study Group.
Newman NJ, et al.
Brain. 2023 Apr 19;146(4):1328-1341. doi: 10.1093/brain/awac421.
Brain. 2023.
PMID: 36350566
Free PMC article.
Clinical Trial.