Nusinersen efficacy data for 24-month in type 2 and 3 spinal muscular atrophy.
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Ann Clin Transl Neurol. 2022 Mar;9(3):404-409. doi: 10.1002/acn3.51514. Epub 2022 Feb 15.
Ann Clin Transl Neurol. 2022.
PMID: 35166467
Free PMC article.