Base-editing corrects metabolic abnormalities in a humanized mouse model for glycogen storage disease type-Ia.
Arnaoutova I, Aratyn-Schaus Y, Zhang L, Packer MS, Chen HD, Lee C, Gautam S, Gregoire FM, Leboeuf D, Boule S, Fernandez TP, Huang V, Cheng LI, Lung G, Bannister B, Decker J, Leete T, Shuang LS, Bock C, Kothiyal P, Grayson P, Mok KW, Quinn JJ, Young L, Barrera L, Ciaramella G, Mansfield BC, Chou JY.
Arnaoutova I, et al. Among authors: fernandez tp.
Nat Commun. 2024 Nov 10;15(1):9729. doi: 10.1038/s41467-024-54108-1.
Nat Commun. 2024.
PMID: 39523369
Free PMC article.