Minimal Essential Human Factor VIII Alterations Enhance Secretion and Gene Therapy Efficiency.
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Cao W, et al. Among authors: xiao w.
Mol Ther Methods Clin Dev. 2020 Oct 22;19:486-495. doi: 10.1016/j.omtm.2020.10.013. eCollection 2020 Dec 11.
Mol Ther Methods Clin Dev. 2020.
PMID: 33313336
Free PMC article.