Gene correction of a duchenne muscular dystrophy mutation by meganuclease-enhanced exon knock-in.
Popplewell L, Koo T, Leclerc X, Duclert A, Mamchaoui K, Gouble A, Mouly V, Voit T, Pâques F, Cédrone F, Isman O, Yáñez-Muñoz RJ, Dickson G.
Popplewell L, et al. Among authors: dickson g.
Hum Gene Ther. 2013 Jul;24(7):692-701. doi: 10.1089/hum.2013.081.
Hum Gene Ther. 2013.
PMID: 23790397