Amelioration of metabolic and behavioral defects through base editing in the PahR408W phenylketonuria mouse model.
Yin S, Gao L, Sun X, Zhang M, Gao H, Chen X, Zhang D, Ming X, Yang L, Hu Y, Chen X, Liu M, Zhan X, Guan Y, Wang L, Han L, Zhu P, Li D.
Yin S, et al. Among authors: sun x.
Mol Ther. 2024 Nov 25:S1525-0016(24)00759-7. doi: 10.1016/j.ymthe.2024.11.032. Online ahead of print.
Mol Ther. 2024.
PMID: 39600089