Trilineage hematopoietic toxicity associated with valproic acid therapy

J Pediatr Hematol Oncol. 1997 Jan-Feb;19(1):73-6. doi: 10.1097/00043426-199701000-00011.

Abstract

Purpose: Sodium valproate is commonly used as an anticonvulsant for patients with refractory epilepsy. Hematopoietic toxicity involving platelets or erythrocytes has been previously described, as well as a few cases of generalized bone marrow suppression.

Patients and methods: We report an infant receiving sodium valproate who developed severe anemia and thrombocytopenia, numerous circulating immature myeloid cells, and a coagulopathy. Bone marrow aspirate revealed approximately 40% abnormal promyelocytes, and the initial clinical and pathologic interpretation was consistent with the diagnosis of acute promyelocytic leukemia.

Results: Antineoplastic therapy was withheld while valproate was weaned. All hematopoietic abnormalities resolved after valproate therapy was discontinued.

Conclusion: This report expands the clinical spectrum of hematopoietic toxicity associated with sodium valproate. Drug toxicity should be considered in any patient on valproate who develops hematopoietic abnormalities.

Publication types

  • Case Reports

MeSH terms

  • Cell Lineage / drug effects*
  • Child
  • Female
  • GABA Agents / adverse effects*
  • GABA Agents / therapeutic use
  • Hematopoiesis / drug effects*
  • Hematopoietic Stem Cells / drug effects
  • Hematopoietic Stem Cells / pathology*
  • Humans
  • Leukemia, Promyelocytic, Acute / drug therapy*
  • Valproic Acid / adverse effects*
  • Valproic Acid / therapeutic use

Substances

  • GABA Agents
  • Valproic Acid