Mitochondrial encephalomyopathy: variable clinical expression within a single kindred

J Neurol Neurosurg Psychiatry. 1993 Aug;56(8):900-5. doi: 10.1136/jnnp.56.8.900.

Abstract

The clinical manifestations of mitochondrial encephalomyopathy are described in four generations of a single kindred. The age of onset of major neurological disturbance varied from 3-70 years. In some patients, deafness was the only manifestation; in others, recurrent bouts of status epilepticus associated with focal neurological deficits and headache, caused severe disability or death. Examples of all three adult forms of mitochondrial encephalomyopathy: MELAS, MERFF and Kearns Sayre syndrome, were represented within the kindred. Associated features included deafness, short stature, non-insulin-dependent diabetes mellitus, migraine, peptic ulceration and severe constipation. The nt 3243 A-G MELAS mutation was detected in two members of the kindred. This study highlights the diversity of clinical expression of a mitochondrial mutation within a single kindred.

Publication types

  • Case Reports

MeSH terms

  • Adolescent
  • Adult
  • Aged
  • Brain / diagnostic imaging
  • Child, Preschool
  • DNA / analysis
  • Female
  • Humans
  • Male
  • Middle Aged
  • Mitochondrial Encephalomyopathies / diagnostic imaging
  • Mitochondrial Encephalomyopathies / genetics*
  • Mitochondrial Encephalomyopathies / pathology
  • Muscles / pathology
  • Muscles / ultrastructure
  • Pedigree
  • Tomography, X-Ray Computed

Substances

  • DNA