Development of CD33-Targeted Dual Drug-Loaded Nanoparticles for the Treatment of Pediatric Acute Myeloid Leukemia

Biomacromolecules. 2024 Oct 14;25(10):6503-6514. doi: 10.1021/acs.biomac.4c00672. Epub 2024 Sep 5.

Abstract

Paediatric acute myeloid leukemia (AML) is a heterogeneous hematological malignancy still heavily reliant on traditional chemotherapeutic approaches. Combination treatments have shown to be a superior approach, but their success is often hindered by side effects and different drugs' pharmacokinetics. Here, we investigated ABT-737 and Purvalanol A as a potential drug pairing for pediatric AML and described the development of CD33-targeted polymeric nanoparticles (NPs) to enable their simultaneous targeted codelivery. Separate drug encapsulation within poly(lactic-co-glycolic acid) (PLGA) NPs was optimized prior to coencapsulation of both drugs at a synergistic ratio in PEGylated PLGA NPs. The therapeutic effects of formulations were evaluated in a panel of pediatric AML cells, and dual drug-loaded NPs (dual NPs) demonstrated significantly enhanced apoptotic cell death. Moreover, conjugation to gemtuzumab resulted in improved NP binding and internalization in CD33-positive cells. Finally, CD33-targeted dual-loaded NPs showed enhanced cytotoxicity to CD33-positive AML cells via CD33-mediated targeted drug delivery.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Apoptosis / drug effects
  • Biphenyl Compounds / chemistry
  • Biphenyl Compounds / pharmacology
  • Cell Line, Tumor
  • Child
  • Drug Carriers / chemistry
  • Drug Delivery Systems / methods
  • Gemtuzumab / chemistry
  • Gemtuzumab / pharmacology
  • Humans
  • Leukemia, Myeloid, Acute* / drug therapy
  • Nanoparticles* / chemistry
  • Nitrophenols / chemistry
  • Nitrophenols / pharmacology
  • Piperazines / administration & dosage
  • Piperazines / chemistry
  • Piperazines / pharmacology
  • Polylactic Acid-Polyglycolic Acid Copolymer / chemistry
  • Sialic Acid Binding Ig-like Lectin 3*
  • Sulfonamides / administration & dosage
  • Sulfonamides / chemistry
  • Sulfonamides / pharmacology

Substances

  • Sialic Acid Binding Ig-like Lectin 3
  • CD33 protein, human
  • Sulfonamides
  • Piperazines
  • ABT-737
  • Biphenyl Compounds
  • Nitrophenols
  • Polylactic Acid-Polyglycolic Acid Copolymer
  • Gemtuzumab
  • Drug Carriers