Structural basis for selectivity and antagonism in extracellular GPCR-nanobodies

Nat Commun. 2024 May 30;15(1):4611. doi: 10.1038/s41467-024-49000-x.

Abstract

G protein-coupled receptors (GPCRs) are pivotal therapeutic targets, but their complex structure poses challenges for effective drug design. Nanobodies, or single-domain antibodies, have emerged as a promising therapeutic strategy to target GPCRs, offering advantages over traditional small molecules and antibodies. However, an incomplete understanding of the structural features enabling GPCR-nanobody interactions has limited their development. In this study, we investigate VUN701, a nanobody antagonist targeting the atypical chemokine receptor 3 (ACKR3). We determine that an extended CDR3 loop is required for ACKR3 binding. Uncommon in most nanobodies, an extended CDR3 is prevalent in GPCR-targeting nanobodies. Combining experimental and computational approaches, we map an inhibitory ACKR3-VUN701 interface and define a distinct conformational mechanism for GPCR inactivation. Our results provide insights into class A GPCR-nanobody selectivity and suggest a strategy for the development of these new therapeutic tools.

MeSH terms

  • Animals
  • HEK293 Cells
  • Humans
  • Protein Binding
  • Receptors, CXCR* / antagonists & inhibitors
  • Receptors, CXCR* / chemistry
  • Receptors, CXCR* / genetics
  • Receptors, CXCR* / metabolism
  • Receptors, G-Protein-Coupled / antagonists & inhibitors
  • Receptors, G-Protein-Coupled / chemistry
  • Receptors, G-Protein-Coupled / metabolism
  • Single-Domain Antibodies* / chemistry
  • Single-Domain Antibodies* / metabolism

Substances

  • Single-Domain Antibodies
  • Receptors, CXCR
  • ACKR3 protein, human
  • Receptors, G-Protein-Coupled