Clinical, paraclinical and outcome features of 166 patients with acute anti-GQ1b antibody syndrome

J Neurol. 2024 Aug;271(8):4982-4990. doi: 10.1007/s00415-024-12410-4. Epub 2024 May 20.

Abstract

Background & purpose: In this retrospective study, we aimed at defining the clinical, paraclinical and outcome features of acute neurological syndromes associated with anti-GQ1b antibodies.

Results: We identified 166 patients with neurological symptoms appearing in less than 1 month and anti-GQ1b antibodies in serum between 2012 and 2022. Half were female (51%), mean age was 50 years (4-90), and the most frequent clinical features were areflexia (80% of patients), distal upper and lower limbs sensory symptoms (78%), ophthalmoplegia (68%), sensory ataxia (67%), limb muscle weakness (45%) and bulbar weakness (45%). Fifty-three patients (32%) presented with complete (21%) and incomplete (11%) Miller Fisher syndrome (MFS), thirty-six (22%) with Guillain-Barre syndrome (GBS), one (0.6%) with Bickerstaff encephalitis (BE), and seventy-three (44%) with mixed MFS, GBS & BE clinical features. Nerve conduction studies were normal in 46% of cases, showed demyelination in 28%, and axonal loss in 23%. Anti-GT1a antibodies were found in 56% of cases, increased cerebrospinal fluid protein content in 24%, and Campylobacter jejuni infection in 7%. Most patients (83%) were treated with intravenous immunoglobulins, and neurological recovery was complete in 69% of cases at 1 year follow-up. One patient died, and 15% of patients relapsed. Age > 70 years, initial Intensive Care Unit (ICU) admission, and absent anti-GQ1b IgG antibodies were predictors of incomplete recovery at 12 months. No predictors of relapse were identified.

Conclusion: This study from Western Europe shows acute anti-GQ1b antibody syndrome presents with a large clinical phenotype, a good outcome in 2/3 of cases, and frequent relapses.

Keywords: Anti-GQ1b antibodies; Bickerstaff’s brainstem encephalitis; Guillain–Barre syndrome; Miller-Fisher syndrome.

MeSH terms

  • Adolescent
  • Adult
  • Aged
  • Aged, 80 and over
  • Autoantibodies* / blood
  • Autoantibodies* / cerebrospinal fluid
  • Child
  • Child, Preschool
  • Female
  • Gangliosides* / immunology
  • Guillain-Barre Syndrome / blood
  • Guillain-Barre Syndrome / diagnosis
  • Guillain-Barre Syndrome / immunology
  • Guillain-Barre Syndrome / physiopathology
  • Humans
  • Male
  • Middle Aged
  • Miller Fisher Syndrome* / blood
  • Miller Fisher Syndrome* / diagnosis
  • Miller Fisher Syndrome* / physiopathology
  • Retrospective Studies
  • Young Adult

Substances

  • Gangliosides
  • GQ1b ganglioside
  • Autoantibodies