Specificity of CRISPR-Cas9 Editing in Exagamglogene Autotemcel

N Engl J Med. 2024 May 9;390(18):1723-1725. doi: 10.1056/NEJMc2313119. Epub 2024 Apr 24.
No abstract available

Publication types

  • Letter

MeSH terms

  • Antigens, CD34
  • CRISPR-Associated Protein 9
  • CRISPR-Cas Systems*
  • Cell- and Tissue-Based Therapy* / adverse effects
  • Cell- and Tissue-Based Therapy* / methods
  • Gene Editing* / methods
  • Hematopoietic Stem Cell Transplantation* / methods
  • Hematopoietic Stem Cells
  • Humans
  • Postoperative Complications / genetics
  • Postoperative Complications / prevention & control