Impact of trial attrition rates on treatment effect estimates in chronic inflammatory diseases: A meta-epidemiological study

Res Synth Methods. 2024 Jul;15(4):561-575. doi: 10.1002/jrsm.1708. Epub 2024 Feb 13.

Abstract

The objective of this meta-epidemiological study was to explore the impact of attrition rates on treatment effect estimates in randomised trials of chronic inflammatory diseases (CID) treated with biological and targeted synthetic disease-modifying drugs. We sampled trials from Cochrane reviews. Attrition rates and primary endpoint results were retrieved from trial publications; Odds ratios (ORs) were calculated from the odds of withdrawing in the experimental intervention compared to the control comparison groups (i.e., differential attrition), as well as the odds of achieving a clinical response (i.e., the trial outcome). Trials were combined using random effects restricted maximum likelihood meta-regression models and associations between estimates of treatment effects and attrition rates were analysed. From 37 meta-analyses, 179 trials were included, and 163 were analysed (301 randomised comparisons; n = 62,220 patients). Overall, the odds of withdrawal were lower in the experimental compared to control groups (random effects summary OR = 0.45, 95% CI, 0.41-0.50). The corresponding overall treatment effects were large (random effects summary OR = 4.43, 95% CI 3.92-4.99) with considerable heterogeneity across interventions and clinical specialties (I2 = 85.7%). The ORs estimating treatment effect showed larger treatment benefits when the differential attrition was more prominent with more attrition in the control group (OR = 0.73, 95% CI 0.55-0.96). Higher attrition rates from the control arm are associated with larger estimated benefits of treatments with biological or targeted synthetic disease-modifying drugs in CID trials; differential attrition may affect estimates of treatment benefit in randomised trials.

Keywords: attrition bias; biological therapy; inflammatory bowel disease; meta‐research; psoriasis; rheumatology.

Publication types

  • Meta-Analysis

MeSH terms

  • Chronic Disease
  • Epidemiologic Studies
  • Humans
  • Inflammation* / drug therapy
  • Likelihood Functions
  • Odds Ratio
  • Patient Dropouts
  • Randomized Controlled Trials as Topic*
  • Research Design
  • Treatment Outcome