Molecular determinants of ligand efficacy and potency in GPCR signaling

Science. 2023 Dec 22;382(6677):eadh1859. doi: 10.1126/science.adh1859. Epub 2023 Dec 22.

Abstract

Heterotrimeric guanine nucleotide-binding protein (G protein)-coupled receptors (GPCRs) bind to extracellular ligands and drugs and modulate intracellular responses through conformational changes. Despite their importance as drug targets, the molecular origins of pharmacological properties such as efficacy (maximum signaling response) and potency (the ligand concentration at half-maximal response) remain poorly understood for any ligand-receptor-signaling system. We used the prototypical adrenaline-β2 adrenergic receptor-G protein system to reveal how specific receptor residues decode and translate the information encoded in a ligand to mediate a signaling response. We present a data science framework to integrate pharmacological and structural data to uncover structural changes and allosteric networks relevant for ligand pharmacology. These methods can be tailored to study any ligand-receptor-signaling system, and the principles open possibilities for designing orthosteric and allosteric compounds with defined signaling properties.

MeSH terms

  • Adrenergic beta-2 Receptor Agonists* / chemistry
  • Adrenergic beta-2 Receptor Agonists* / pharmacology
  • Allosteric Regulation
  • Bioluminescence Resonance Energy Transfer Techniques
  • Biosensing Techniques
  • Humans
  • Ligands
  • Protein Conformation
  • Receptors, Adrenergic, beta-2* / chemistry
  • Receptors, Adrenergic, beta-2* / genetics
  • Signal Transduction

Substances

  • Adrenergic beta-2 Receptor Agonists
  • Ligands
  • Receptors, Adrenergic, beta-2