Inhibition of FGFR Signaling by Targeting FGF/FGFR Extracellular Interactions: Towards the Comprehension of the Molecular Mechanism through NMR Approaches

Int J Mol Sci. 2022 Sep 17;23(18):10860. doi: 10.3390/ijms231810860.

Abstract

NMR-based approaches play a pivotal role in providing insight into molecular recognition mechanisms, affording the required atomic-level description and enabling the identification of promising inhibitors of protein-protein interactions. The aberrant activation of the fibroblast growth factor 2 (FGF2)/fibroblast growth factor receptor (FGFR) signaling pathway drives several pathologies, including cancer development, metastasis formation, resistance to therapy, angiogenesis-driven pathologies, vascular diseases, and viral infections. Most FGFR inhibitors targeting the intracellular ATP binding pocket of FGFR have adverse effects, such as limited specificity and relevant toxicity. A viable alternative is represented by targeting the FGF/FGFR extracellular interactions. We previously identified a few small-molecule inhibitors acting extracellularly, targeting FGFR or FGF. We have now built a small library of natural and synthetic molecules that potentially act as inhibitors of FGF2/FGFR interactions to improve our understanding of the molecular mechanisms of inhibitory activity. Here, we provide a comparative analysis of the interaction mode of small molecules with the FGF2/FGFR complex and the single protein domains. DOSY and residue-level NMR analysis afforded insights into the capability of the potential inhibitors to destabilize complex formation, highlighting different mechanisms of inhibition of FGF2-induced cell proliferation.

Keywords: DOSY; NMR; allosteric inhibitors; dobesilate; fibroblast growth factor; resveratrol; rosmarinic acid.

MeSH terms

  • Adenosine Triphosphate / pharmacology
  • Comprehension
  • Fibroblast Growth Factor 2* / pharmacology
  • Fibroblast Growth Factors / metabolism
  • Humans
  • Neoplasms* / metabolism
  • Receptors, Fibroblast Growth Factor / metabolism
  • Signal Transduction

Substances

  • Receptors, Fibroblast Growth Factor
  • Fibroblast Growth Factor 2
  • Fibroblast Growth Factors
  • Adenosine Triphosphate

Grants and funding

This research was partly funded by the Italian Association for Cancer Research (AIRC, grant number IG2018-21359 to G.T.).