CHARGE syndrome protein CHD7 regulates epigenomic activation of enhancers in granule cell precursors and gyrification of the cerebellum

Nat Commun. 2021 Sep 29;12(1):5702. doi: 10.1038/s41467-021-25846-3.

Abstract

Regulation of chromatin plays fundamental roles in the development of the brain. Haploinsufficiency of the chromatin remodeling enzyme CHD7 causes CHARGE syndrome, a genetic disorder that affects the development of the cerebellum. However, how CHD7 controls chromatin states in the cerebellum remains incompletely understood. Using conditional knockout of CHD7 in granule cell precursors in the mouse cerebellum, we find that CHD7 robustly promotes chromatin accessibility, active histone modifications, and RNA polymerase recruitment at enhancers. In vivo profiling of genome architecture reveals that CHD7 concordantly regulates epigenomic modifications associated with enhancer activation and gene expression of topologically-interacting genes. Genome and gene ontology studies show that CHD7-regulated enhancers are associated with genes that control brain tissue morphogenesis. Accordingly, conditional knockout of CHD7 triggers a striking phenotype of cerebellar polymicrogyria, which we have also found in a case of CHARGE syndrome. Finally, we uncover a CHD7-dependent switch in the preferred orientation of granule cell precursor division in the developing cerebellum, providing a potential cellular basis for the cerebellar polymicrogyria phenotype upon loss of CHD7. Collectively, our findings define epigenomic regulation by CHD7 in granule cell precursors and identify abnormal cerebellar patterning upon CHD7 depletion, with potential implications for our understanding of CHARGE syndrome.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • CHARGE Syndrome / genetics*
  • CHARGE Syndrome / pathology
  • Cell Division / genetics
  • Cerebellum / growth & development*
  • Cerebellum / pathology
  • Chromatin Assembly and Disassembly
  • DNA Helicases / genetics
  • DNA-Binding Proteins / genetics
  • DNA-Binding Proteins / metabolism*
  • Disease Models, Animal
  • Enhancer Elements, Genetic
  • Epigenesis, Genetic
  • Gene Expression Regulation, Developmental*
  • Histone Code
  • Humans
  • Infant
  • Mice
  • Mice, Knockout
  • Mutation
  • Neural Stem Cells / metabolism
  • Neurons / metabolism
  • Polymicrogyria / genetics*
  • Polymicrogyria / pathology
  • RNA-Seq

Substances

  • Chd7 protein, mouse
  • DNA-Binding Proteins
  • DNA Helicases
  • CHD7 protein, human