Discovery of Sisunatovir (RV521), an Inhibitor of Respiratory Syncytial Virus Fusion

J Med Chem. 2021 Apr 8;64(7):3658-3676. doi: 10.1021/acs.jmedchem.0c01882. Epub 2021 Mar 17.

Abstract

RV521 is an orally bioavailable inhibitor of respiratory syncytial virus (RSV) fusion that was identified after a lead optimization process based upon hits that originated from a physical property directed hit profiling exercise at Reviral. This exercise encompassed collaborations with a number of contract organizations with collaborative medicinal chemistry and virology during the optimization phase in addition to those utilized as the compound proceeded through preclinical and clinical evaluation. RV521 exhibited a mean IC50 of 1.2 nM against a panel of RSV A and B laboratory strains and clinical isolates with antiviral efficacy in the Balb/C mouse model of RSV infection. Oral bioavailability in preclinical species ranged from 42 to >100% with evidence of highly efficient penetration into lung tissue. In healthy adult human volunteers experimentally infected with RSV, a potent antiviral effect was observed with a significant reduction in viral load and symptoms compared to placebo.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antiviral Agents / chemical synthesis
  • Antiviral Agents / pharmacokinetics
  • Antiviral Agents / pharmacology*
  • Benzimidazoles / chemical synthesis
  • Benzimidazoles / pharmacokinetics
  • Benzimidazoles / pharmacology*
  • Biological Availability
  • Cell Line, Tumor
  • Clinical Trials as Topic
  • Drug Discovery
  • Humans
  • Microbial Sensitivity Tests
  • Protein Binding
  • Respiratory Syncytial Virus, Human / drug effects*
  • Viral Fusion Proteins / metabolism
  • Virus Internalization / drug effects*

Substances

  • Antiviral Agents
  • Benzimidazoles
  • F protein, human respiratory syncytial virus
  • Viral Fusion Proteins
  • sisunatovir