Response of human melanoma cell lines to interferon-beta gene transfer mediated by a modified adenoviral vector

Sci Rep. 2020 Oct 21;10(1):17893. doi: 10.1038/s41598-020-74826-y.

Abstract

Since melanomas often retain wild type p53, we developed an adenoviral vector, AdRGD-PG, which provides robust transduction and transgene expression in response to p53. Previously, this vector was used for interferon-β gene transfer in mouse models of melanoma, resulting in control of tumor progression, but limited cell killing. Here, the AdRGD-PG-hIFNβ vector encoding the human interferon-β cDNA (hIFNβ) was used to transduce human melanoma cell lines SK-MEL-05 and SK-MEL-147 (both wild type p53). In vitro, cell death was induced in more than 80% of the cells and correlated with elevated annexinV staining and caspase 3/7 activity. Treatment with hIFNβ promoted cell killing in neighboring, non-transduced cells, thus revealing a bystander effect. In situ gene therapy resulted in complete inhibition of tumor progression for SK-MEL-147 when using nude mice with no evidence of hepatotoxicity. However, the response in Nod-Scid mice was less robust. For SK-MEL-05, tumor inhibition was similar in nude and Nod-Scid mice and was less efficient than seen for SK-MEL-147, indicating both cell type and host specific responses. The AdRGD-PG-hIFNβ vector provides extensive killing of human melanoma cells in vitro and a potent anti-tumor effect in vivo. This study provides a critical advance in the development of our melanoma gene therapy approach.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adenoviridae*
  • Animals
  • Annexin A5 / metabolism
  • Caspase 3 / metabolism
  • Cell Line, Tumor
  • DNA, Complementary
  • Gene Transfer Techniques*
  • Genetic Therapy
  • Genetic Vectors*
  • Humans
  • Interferon-beta / genetics*
  • Melanoma / genetics*
  • Melanoma / pathology*
  • Melanoma / therapy
  • Mice, Inbred NOD
  • Mice, Nude
  • Mice, SCID
  • Molecular Targeted Therapy
  • Tumor Suppressor Protein p53

Substances

  • Annexin A5
  • DNA, Complementary
  • Tumor Suppressor Protein p53
  • Interferon-beta
  • Caspase 3