Report on the workshop: Meaningful outcome measures for Duchenne muscular dystrophy, London, UK, 30-31 January 2017
Neuromuscul Disord
.
2018 Aug;28(8):690-701.
doi: 10.1016/j.nmd.2018.05.013.
Epub 2018 Jun 6.
Authors
Volker Straub
1
,
Eugenio Mercuri
2
;
DMD outcome measure study group
Collaborators
DMD outcome measure study group
:
Annemieke Aartsma-Rus
3
,
Dimitrios Athanasiou
4
,
Pavel Balabanov
5
,
Filippo Buccella
6
,
Didier Caizergues
7
,
Pierre Carlier
8
,
Emily Crossley
9
,
Anne M Connolly
10
,
Tina Duong
11
,
Dirk Fischer
12
,
Pat Furlong
13
,
Nathalie Goemans
14
,
Imelda de Groot
15
,
Michela Guglieri
16
,
Erik Henricson
17
,
Alex Johnson
9
,
Hermien E Kan
3
,
Anna Mayhew
16
,
Elena Mazzone
18
,
Craig M McDonald
17
,
Eugenio Mercuri
18
,
Francesco Muntoni
19
,
Erik H Niks
3
,
Laurent Servais
20
,
Cathy Turner
16
,
Thomas Voit
19
,
Elizabeth Vroom
21
,
Glenn Walter
22
Affiliations
1
Institute of Genetic Medicine, Newcastle University John Walton Muscular Dystrophy Research Centre, Newcastle, UK.
2
Pediatric Neurology Unit, Fondazione Policlinico Gemelli, Università Cattolica del Sacro Cuore, Rome, Italy. Electronic address: eugeniomaria.mercuri@unicatt.it.
3
(Leiden, The Netherlands).
4
(MDA Hellas, Greece).
5
(EMA, London UK).
6
(Parent Project Onlus, Italy).
7
(Évry, France).
8
(Paris, France).
9
(Duchenne UK, UK).
10
(Missouri, USA).
11
(Stanford, USA).
12
(Basel, Switzerland).
13
(PPMD, USA).
14
(Leuven, Belgium).
15
(Nijmegen, The Netherlands).
16
(Newcastle, UK).
17
(California, USA).
18
(Rome, Italy).
19
(London, UK).
20
(Liege, Belgium).
21
(UPPMD, The Netherlands).
22
(Florida, USA).
PMID:
30033203
DOI:
10.1016/j.nmd.2018.05.013
No abstract available
Publication types
Congress
Research Support, Non-U.S. Gov't
MeSH terms
Humans
Muscular Dystrophy, Duchenne*
Outcome Assessment, Health Care