Hypersensitivity reactions to therapeutic monoclonal antibodies: Phenotypes and endotypes

J Allergy Clin Immunol. 2018 Jul;142(1):159-170.e2. doi: 10.1016/j.jaci.2018.02.018. Epub 2018 Mar 5.

Abstract

Background: The increasing use of mAbs has led to a rise in hypersensitivity reactions (HSRs), which prevent their use as first-line therapy. HSRs' symptoms, diagnostic tools, and directed management approaches have not been standardized.

Objective: We propose a novel evidence-based classification of HSRs to mAbs, based on the clinical phenotypes, underlying endotypes and biomarkers, as well as their management with desensitization.

Methods: Phenotypes, endotypes, and biomarkers of HSRs to 16 mAbs for 104 patients were described and compared with the outcomes of 526 subcutaneous and intravenous desensitizations.

Results: Initial reactions presented with 4 patterns: type I-like reactions (63%), cytokine-release reactions (13%), mixed reactions (21%), and delayed type IV reactions (3%). In contrast, of the 23% breakthrough HSRs during desensitization, 52% were cytokine-release reactions, 32% were type 1, 12% were mixed, and 4% were type I with delayed type IV. Skin testing to 10 mAbs in 58 patients was positive in 41% of patients. Serum tryptase was elevated in 1 patient and IL-6 was elevated in 8 patients during desensitization and was associated with a cytokine-release phenotype.

Conclusions: HSRs to mAbs can be defined as type I, cytokine-release, mixed (type I/cytokine-release), and type IV reactions, which are identified by biomarkers such as skin test, tryptase, and IL-6. These phenotypes can be used to improve personalized and precision medicine when diagnosing HSRs to mAbs and providing management recommendations with desensitization. Desensitization provides a safe and effective retreatment option to remain on culprit mAbs as first-line therapy.

Keywords: IL-6; Monoclonal antibody; biomarkers; desensitization; endotype; hypersensitivity reaction; phenotype; precision medicine; skin testing; tryptase.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Aged
  • Aged, 80 and over
  • Antibodies, Monoclonal / adverse effects*
  • Antibodies, Monoclonal / immunology
  • Desensitization, Immunologic / methods*
  • Drug Hypersensitivity / classification*
  • Drug Hypersensitivity / prevention & control*
  • Female
  • Humans
  • Male
  • Middle Aged
  • Phenotype
  • Retrospective Studies
  • Young Adult

Substances

  • Antibodies, Monoclonal