CHARGEd with neural crest defects

Am J Med Genet C Semin Med Genet. 2017 Dec;175(4):478-486. doi: 10.1002/ajmg.c.31584. Epub 2017 Oct 30.

Abstract

Neural crest cells are highly migratory pluripotent cells that give rise to diverse derivatives including cartilage, bone, smooth muscle, pigment, and endocrine cells as well as neurons and glia. Abnormalities in neural crest-derived tissues contribute to the etiology of CHARGE syndrome, a complex malformation disorder that encompasses clinical symptoms like coloboma, heart defects, atresia of the choanae, retarded growth and development, genital hypoplasia, ear anomalies, and deafness. Mutations in the chromodomain helicase DNA-binding protein 7 (CHD7) gene are causative of CHARGE syndrome and loss-of-function data in different model systems have firmly established a role of CHD7 in neural crest development. Here, we will summarize our current understanding of the function of CHD7 in neural crest development and discuss possible links of CHARGE syndrome to other developmental disorders.

Keywords: CHARGE syndrome; CHD7; chromatin remodeling; neural crest; neural crest development.

Publication types

  • Review
  • Research Support, Non-U.S. Gov't
  • Research Support, N.I.H., Extramural

MeSH terms

  • Adenosine Triphosphate / metabolism
  • Animals
  • CHARGE Syndrome / diagnosis*
  • CHARGE Syndrome / etiology*
  • CHARGE Syndrome / metabolism
  • Chromatin Assembly and Disassembly
  • DNA Helicases / genetics
  • DNA Helicases / metabolism
  • DNA-Binding Proteins / genetics
  • DNA-Binding Proteins / metabolism
  • Disease Models, Animal
  • Humans
  • Multiprotein Complexes / metabolism
  • Mutation
  • Neural Crest / abnormalities*
  • Phenotype*
  • Protein Binding

Substances

  • DNA-Binding Proteins
  • Multiprotein Complexes
  • Adenosine Triphosphate
  • DNA Helicases
  • CHD7 protein, human