Therapeutic miR-21 Silencing Ameliorates Diabetic Kidney Disease in Mice

Mol Ther. 2017 Jan 4;25(1):165-180. doi: 10.1016/j.ymthe.2016.08.001. Epub 2017 Jan 4.

Abstract

Diabetic nephropathy is the main cause of end-stage renal disease. MicroRNAs are powerful regulators of the genome, and global expression profiling revealed miR-21 to be among the most highly regulated microRNAs in kidneys of mice with diabetic nephropathy. In kidney biopsies of diabetic patients, miR-21 correlated with tubulointerstitial injury. In situ PCR analysis showed a specific enrichment of miR-21 in glomerular cells. We identified cell division cycle 25a (Cdc25a) and cyclin-dependent kinase 6 (Cdk6) as novel miR-21 targets in mesangial cells. miR-21-mediated repression of Cdc25a and Cdk6 resulted in impaired cell cycle progression and subsequent mesangial cell hypertrophy. miR-21 increased podocyte motility by regulating phosphatase and tensin homolog (Pten). miR-21 antagonism in vitro and in vivo in streptozotocin-induced diabetic mice decreased mesangial expansion, interstitial fibrosis, macrophage infiltration, podocyte loss, albuminuria, and fibrotic- and inflammatory gene expression. In conclusion, miR-21 antagonism rescued various functional and structural parameters in mice with diabetic nephropathy and, thus, might be a viable option in the treatment of patients with diabetic kidney disease.

Keywords: TGF-β; cell-cycle regulators; diabetic nephropathy; mesangial hypertrophy; miR-21; microRNA; podocyte motility.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Cell Cycle Checkpoints / genetics
  • Cell Movement
  • Cluster Analysis
  • Cyclin-Dependent Kinase 6 / genetics
  • Diabetes Mellitus, Experimental
  • Diabetic Nephropathies / genetics*
  • Diabetic Nephropathies / metabolism
  • Diabetic Nephropathies / pathology
  • Diabetic Nephropathies / therapy
  • Disease Models, Animal
  • Fibrosis
  • Gene Expression Profiling
  • Gene Expression Regulation
  • Gene Silencing*
  • Inflammation / genetics
  • Inflammation / metabolism
  • Inflammation / pathology
  • Kidney Glomerulus / metabolism
  • Kidney Glomerulus / pathology
  • Mesangial Cells / metabolism
  • Mice
  • MicroRNAs / genetics*
  • Podocytes / metabolism
  • RNA Interference
  • cdc25 Phosphatases / genetics

Substances

  • MIRN21 microRNA, mouse
  • MicroRNAs
  • Cyclin-Dependent Kinase 6
  • Cdc25a protein, mouse
  • cdc25 Phosphatases