Stratification and therapeutic potential of PML in metastatic breast cancer

Nat Commun. 2016 Aug 24:7:12595. doi: 10.1038/ncomms12595.

Abstract

Patient stratification has been instrumental for the success of targeted therapies in breast cancer. However, the molecular basis of metastatic breast cancer and its therapeutic vulnerabilities remain poorly understood. Here we show that PML is a novel target in aggressive breast cancer. The acquisition of aggressiveness and metastatic features in breast tumours is accompanied by the elevated PML expression and enhanced sensitivity to its inhibition. Interestingly, we find that STAT3 is responsible, at least in part, for the transcriptional upregulation of PML in breast cancer. Moreover, PML targeting hampers breast cancer initiation and metastatic seeding. Mechanistically, this biological activity relies on the regulation of the stem cell gene SOX9 through interaction of PML with its promoter region. Altogether, we identify a novel pathway sustaining breast cancer aggressiveness that can be therapeutically exploited in combination with PML-based stratification.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Arsenic Trioxide
  • Arsenicals / pharmacology
  • Breast Neoplasms / metabolism
  • Breast Neoplasms / secondary*
  • Breast Neoplasms / therapy*
  • Cell Line, Tumor
  • Female
  • Gene Knockdown Techniques
  • Humans
  • MCF-7 Cells
  • Mice
  • Neoplasm Invasiveness / genetics
  • Oxides / pharmacology
  • Promoter Regions, Genetic
  • Promyelocytic Leukemia Protein / antagonists & inhibitors*
  • Promyelocytic Leukemia Protein / genetics
  • Promyelocytic Leukemia Protein / metabolism*
  • SOX9 Transcription Factor / genetics
  • STAT3 Transcription Factor / metabolism
  • Xenograft Model Antitumor Assays

Substances

  • Arsenicals
  • Oxides
  • Promyelocytic Leukemia Protein
  • SOX9 Transcription Factor
  • SOX9 protein, human
  • STAT3 Transcription Factor
  • STAT3 protein, human
  • PML protein, human
  • Arsenic Trioxide