Interpretation of an Extended Autoantibody Profile in a Well-Characterized Australian Systemic Sclerosis (Scleroderma) Cohort Using Principal Components Analysis

Arthritis Rheumatol. 2015 Dec;67(12):3234-44. doi: 10.1002/art.39316.

Abstract

Objective: To determine the relationships between systemic sclerosis (SSc)-related autoantibodies, as well as their clinical associations, in a well-characterized Australian patient cohort.

Methods: Serum from 505 Australian SSc patients were analyzed with a commercial line immunoassay (EuroLine; Euroimmun) for autoantibodies to centromere proteins CENP-A and CENP-B, RNA polymerase III (RNAP III; epitopes 11 and 155), the 90-kd nucleolar protein NOR-90, fibrillarin, Th/To, PM/Scl-75, PM/Scl-100, Ku, topoisomerase I (topo I), tripartite motif-containing protein 21/Ro 52, and platelet-derived growth factor receptor. Patient subgroups were identified by hierarchical clustering of the first 2 dimensions of a principal components analysis of quantitative autoantibody scores. Results were compared with detailed clinical data.

Results: A total of 449 of the 505 patients were positive for at least 1 autoantibody by immunoblotting. Heatmap visualization of autoantibody scores, along with principal components analysis clustering, demonstrated strong, mutually exclusive relationships between CENP, RNAP III, and topo I. Five patient clusters were identified: CENP, RNAP III strong, RNAP III weak, topo I, and other. Clinical features associated with CENP, RNAP III, and topo I were consistent with previously published reports concerning limited cutaneous and diffuse cutaneous SSc. A novel finding was the statistical separation of RNAP III into 2 clusters. Patients in the RNAP III strong cluster had an increased risk of gastric antral vascular ectasia, but a lower risk of esophageal dysmotility. Patients in the other cluster were more likely to be male and to have a history of smoking and a history of malignancy, but were less likely to have telangiectasia, Raynaud's phenomenon, and joint contractures.

Conclusion: Five major autoantibody clusters with specific clinical and serologic associations were identified in Australian SSc patients. Subclassification and disease stratification using autoantibodies may have clinical utility, particularly in early disease.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Aged
  • Antigens, Nuclear / immunology
  • Australia
  • Autoantibodies / immunology*
  • Autoantigens / immunology
  • Centromere Protein A
  • Centromere Protein B / immunology
  • Chromosomal Proteins, Non-Histone / immunology
  • Cohort Studies
  • Contracture / etiology
  • Contracture / immunology
  • DNA Topoisomerases, Type I / immunology
  • DNA-Binding Proteins / immunology
  • Esophageal Motility Disorders / etiology
  • Esophageal Motility Disorders / immunology
  • Exoribonucleases / immunology
  • Exosome Multienzyme Ribonuclease Complex / immunology
  • Female
  • Gastric Antral Vascular Ectasia / etiology
  • Gastric Antral Vascular Ectasia / immunology
  • Humans
  • Immunoblotting
  • Ku Autoantigen
  • Male
  • Middle Aged
  • Neoplasms / epidemiology
  • Pol1 Transcription Initiation Complex Proteins / immunology
  • Principal Component Analysis
  • RNA Polymerase III / immunology
  • RNA-Binding Proteins / immunology
  • Raynaud Disease / etiology
  • Raynaud Disease / immunology
  • Receptors, Platelet-Derived Growth Factor / immunology
  • Ribonucleoproteins / immunology
  • Scleroderma, Systemic / complications
  • Scleroderma, Systemic / epidemiology
  • Scleroderma, Systemic / immunology*
  • Sex Factors
  • Smoking / epidemiology
  • Telangiectasis / etiology
  • Telangiectasis / immunology

Substances

  • Antigens, Nuclear
  • Autoantibodies
  • Autoantigens
  • CENPA protein, human
  • CENPB protein, human
  • Centromere Protein A
  • Centromere Protein B
  • Chromosomal Proteins, Non-Histone
  • DNA-Binding Proteins
  • EXOSC9 protein, human
  • Pol1 Transcription Initiation Complex Proteins
  • RNA-Binding Proteins
  • Ribonucleoproteins
  • SS-A antigen
  • fibrillarin
  • transcription factor UBF
  • Receptors, Platelet-Derived Growth Factor
  • RNA Polymerase III
  • Exoribonucleases
  • Exosome Multienzyme Ribonuclease Complex
  • EXOSC10 protein, human
  • Xrcc6 protein, human
  • Ku Autoantigen
  • DNA Topoisomerases, Type I