Cost-effectiveness of extended-release methylphenidate in children and adolescents with attention-deficit/hyperactivity disorder sub-optimally treated with immediate release methylphenidate

PLoS One. 2015 May 29;10(5):e0127237. doi: 10.1371/journal.pone.0127237. eCollection 2015.

Abstract

Background: Attention-Deficit/Hyperactivity Disorder (ADHD) is a common psychiatric disorder in children and adolescents. Immediate-release methylphenidate (IR-MPH) is the medical treatment of first choice. The necessity to use several IR-MPH tablets per day and associated potential social stigma at school often leads to reduced compliance, sub-optimal treatment, and therefore economic loss. Replacement of IR-MPH with a single-dose extended release (ER-MPH) formulation may improve drug response and economic efficiency.

Objective: To evaluate the cost-effectiveness from a societal perspective of a switch from IR-MPH to ER-MPH in patients who are sub-optimally treated.

Methods: A daily Markov-cycle model covering a time-span of 10 years was developed including four different health states: (1) optimal response, (2) sub-optimal response, (3) discontinued treatment, and (4) natural remission. ER-MPH options included methylphenidate osmotic release oral system (MPH-OROS) and Equasym XL/Medikinet CR. Both direct costs and indirect costs were included in the analysis, and effects were expressed as quality-adjusted life years (QALYs). Univariate, multivariate as well as probabilistic sensitivity analysis were conducted and the main outcomes were incremental cost-effectiveness ratios.

Results: Switching sub-optimally treated patients from IR-MPH to MPH-OROS or Equasym XL/Medikinet CR led to per-patient cost-savings of €4200 and €5400, respectively, over a 10-year treatment span. Sensitivity analysis with plausible variations of input parameters resulted in cost-savings in the vast majority of estimations.

Conclusions: This study lends economic support to switching patients with ADHD with suboptimal response to short-acting IR-MPH to long-acting ER-MPH regimens.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Central Nervous System Stimulants / administration & dosage*
  • Central Nervous System Stimulants / therapeutic use
  • Child
  • Cost-Benefit Analysis*
  • Delayed-Action Preparations / administration & dosage
  • Female
  • Humans
  • Male
  • Markov Chains
  • Methylphenidate / administration & dosage*
  • Methylphenidate / therapeutic use
  • Tablets / administration & dosage

Substances

  • Central Nervous System Stimulants
  • Delayed-Action Preparations
  • Tablets
  • Methylphenidate

Grants and funding

All phases of this study were supported by a Netherlands Organisation for Health Research and Development (ZonMW) grant, #836011014. The funders had no role in study design, data collection and analysis, decision to publish, or preparation of the manuscript.