Delivery of oligonucleotides with lipid nanoparticles

Adv Drug Deliv Rev. 2015 Jun 29:87:68-80. doi: 10.1016/j.addr.2015.02.007. Epub 2015 Feb 27.

Abstract

Since their inception in the 1980s, oligonucleotide-based (ON-based) therapeutics have been recognized as powerful tools that can treat a broad spectrum of diseases. The discoveries of novel regulatory methods of gene expression with diverse mechanisms of action are still driving the development of novel ON-based therapeutics. Difficulties in the delivery of this class of therapeutics hinder their in vivo applications, which forces drug delivery systems to be a prerequisite for clinical translation. This review discusses the strategy of using lipid nanoparticles as carriers to deliver therapeutic ONs to target cells in vitro and in vivo. A discourse on how chemical and physical properties of the lipid materials could be utilized during formulation and the resulting effects on delivery efficiency constitutes the major part of this review.

Keywords: Lipid nanoparticles; Lipoplexes; Liposome; Oligonucleotides; Systemic delivery.

Publication types

  • Research Support, N.I.H., Extramural
  • Review

MeSH terms

  • Animals
  • Biological Transport
  • Chemistry, Pharmaceutical
  • Drug Carriers / chemistry*
  • Drug Compounding
  • Drug Liberation
  • Humans
  • Immunotherapy / methods
  • Lipids / chemistry*
  • Liposomes
  • Liver Diseases / drug therapy
  • Liver Diseases / metabolism
  • Lung Diseases / drug therapy
  • Lung Diseases / metabolism
  • Nanoparticles / chemistry*
  • Oligonucleotides / administration & dosage*
  • Oligonucleotides / pharmacokinetics
  • Oligonucleotides / therapeutic use
  • Surface Properties

Substances

  • Drug Carriers
  • Lipids
  • Liposomes
  • Oligonucleotides