High-dose therapy with auto-SCT is feasible in high-risk cardiac amyloidosis

Bone Marrow Transplant. 2015 May;50(5):668-72. doi: 10.1038/bmt.2015.21. Epub 2015 Mar 2.

Abstract

Cardiac involvement in light-chain amyloidosis (AL) predicts poor prognosis and is associated with higher TRM and morbidity during high-dose therapy and auto-SCT (HDT-ASCT). We studied the outcomes of 30 patients with cardiac amyloidosis undergoing HDT-ASCT at our center between January 1998 and March 2012. The median age of the patients was 53 years (range, 36-74) with a median follow-up of 35 months (range, 0.4-97 months). Twenty-seven patients (90%) had more than one organ involved besides the heart with 37% with cardiac stage ⩾3. Melphalan-based conditioning regimen (140-200 mg/m(2)) was used for HDT-ASCT. One-year TRM is 10%. Three-year OS and EFS from HDT-ASCT was 83% and 56.8%, respectively. Cumulative incidence of relapse at 3 years was 38.5%. Negative factors affecting survival included age >60 years, lack of novel induction therapy and BM plasmacytosis >10%. We conclude that HDT-ASCT is well tolerated in patients with high-risk cardiac amyloidosis and can lead to improved overall outcomes.

Publication types

  • Clinical Trial

MeSH terms

  • Adult
  • Aged
  • Amyloidosis* / mortality
  • Amyloidosis* / therapy
  • Autografts
  • Disease-Free Survival
  • Female
  • Follow-Up Studies
  • Heart Diseases* / mortality
  • Heart Diseases* / therapy
  • Humans
  • Male
  • Melphalan / administration & dosage*
  • Middle Aged
  • Myeloablative Agonists / administration & dosage*
  • Recurrence
  • Stem Cell Transplantation*
  • Survival Rate
  • Transplantation Conditioning*

Substances

  • Myeloablative Agonists
  • Melphalan