Virological and preclinical characterization of a dendritic cell targeting, integration-deficient lentiviral vector for cancer immunotherapy

J Immunother. 2015 Feb-Mar;38(2):41-53. doi: 10.1097/CJI.0000000000000067.

Abstract

Dendritic cells (DCs) are essential antigen-presenting cells for the initiation of cytotoxic T-cell responses and therefore attractive targets for cancer immunotherapy. We have developed an integration-deficient lentiviral vector termed ID-VP02 that is designed to deliver antigen-encoding nucleic acids selectively to human DCs in vivo. ID-VP02 utilizes a genetically and glycobiologically engineered Sindbis virus glycoprotein to target human DCs through the C-type lectin DC-SIGN (CD209) and also binds to the homologue murine receptor SIGNR1. Specificity of ID-VP02 for antigen-presenting cells in the mouse was confirmed through biodistribution studies showing that following subcutaneous administration, transgene expression was only detectable at the injection site and the draining lymph node. A single immunization with ID-VP02 induced a high level of antigen-specific, polyfunctional effector and memory CD8 T-cell responses that fully protected against vaccinia virus challenge. Upon homologous readministration, ID-VP02 induced a level of high-quality secondary effector and memory cells characterized by stable polyfunctionality and expression of IL-7Rα. Importantly, a single injection of ID-VP02 also induced robust cytotoxic responses against an endogenous rejection antigen of CT26 colon carcinoma cells and conferred both prophylactic and therapeutic antitumor efficacy. ID-VP02 is the first lentiviral vector which combines integration deficiency with DC targeting and is currently being investigated in a phase I trial in cancer patients.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • Animals
  • CD8-Positive T-Lymphocytes / immunology*
  • Cancer Vaccines*
  • Carcinoma / immunology
  • Carcinoma / therapy*
  • Cell Adhesion Molecules / metabolism
  • Cell Line, Tumor
  • Clinical Trials, Phase I as Topic
  • Colonic Neoplasms / immunology
  • Colonic Neoplasms / therapy*
  • Cytotoxicity, Immunologic
  • Dendritic Cells / immunology*
  • Dendritic Cells / transplantation
  • Dendritic Cells / virology
  • Genetic Engineering
  • Genetic Vectors*
  • Glycoproteins / genetics
  • Glycoproteins / metabolism
  • Humans
  • Immunologic Memory
  • Immunotherapy, Adoptive*
  • Lectins, C-Type / metabolism
  • Lentivirus / genetics*
  • Lymphocyte Activation
  • Mice
  • Mice, Inbred BALB C
  • Mice, Inbred C57BL
  • Protein Binding
  • Receptors, Cell Surface / metabolism
  • Receptors, Interleukin-7 / metabolism
  • Sindbis Virus / genetics*
  • Vaccinia / immunology*
  • Vaccinia virus / immunology*
  • Viral Proteins / genetics
  • Viral Proteins / metabolism
  • Virus Integration / genetics

Substances

  • Cancer Vaccines
  • Cell Adhesion Molecules
  • DC-specific ICAM-3 grabbing nonintegrin
  • Glycoproteins
  • Lectins, C-Type
  • Receptors, Cell Surface
  • Receptors, Interleukin-7
  • Viral Proteins
  • interleukin-7 receptor, alpha chain