Lipid nanoparticles for gene delivery

Adv Genet. 2014:88:13-36. doi: 10.1016/B978-0-12-800148-6.00002-X.

Abstract

Nonviral vectors which offer a safer and versatile alternative to viral vectors have been developed to overcome problems caused by viral carriers. However, their transfection efficacy or level of expression is substantially lower than viral vectors. Among various nonviral gene vectors, lipid nanoparticles are an ideal platform for the incorporation of safety and efficacy into a single delivery system. In this chapter, we highlight current lipidic vectors that have been developed for gene therapy of tumors and other diseases. The pharmacokinetic, toxic behaviors and clinic trials of some successful lipids particles are also presented.

Keywords: Gene delivery; Lipid nanoparticles.

Publication types

  • Research Support, N.I.H., Extramural
  • Review

MeSH terms

  • Clinical Trials as Topic
  • Gene Transfer Techniques*
  • Genetic Therapy / methods*
  • Genetic Vectors / administration & dosage
  • Genetic Vectors / pharmacokinetics*
  • Humans
  • Lipids / administration & dosage
  • Lipids / chemistry*
  • Lipids / pharmacokinetics*
  • Liver Diseases / genetics
  • Liver Diseases / therapy
  • Nanoparticles / administration & dosage*
  • Nanoparticles / chemistry
  • Nanoparticles / toxicity
  • Neoplasms / genetics
  • Neoplasms / therapy
  • Tissue Distribution

Substances

  • Lipids