[Carriers of fragile X syndrome can present with a broad spectrum of clinical disorders]

Ugeskr Laeger. 2014 Jun 23;176(26):V02140099.
[Article in Danish]

Abstract

Fragile X syndrome, fragile X-associated tremor/ataxia syndrome (FXTAS) and fragile X-associated primary ovarian insufficiency (FXPOI) are three clinically distinct disorders caused by expansions of a CGG repeat sequence in the non-coding part of the FMR1. FXTAS and FXPOI are seen in carriers of smaller repeat expansions (55-200). Carriers were for many years thought to be clinically unaffected, but along with the discovery of FXPOI and FXTAS a growing number of additional clinical manifestations have been identified. We wish to make Danish physicians more aware of these conditions which we review in this paper.

Publication types

  • English Abstract
  • Review

MeSH terms

  • Ataxia / diagnosis
  • Ataxia / genetics
  • Female
  • Fragile X Mental Retardation Protein / genetics
  • Fragile X Syndrome / diagnosis*
  • Fragile X Syndrome / genetics
  • Humans
  • Male
  • Primary Ovarian Insufficiency / diagnosis
  • Primary Ovarian Insufficiency / genetics
  • Tremor / diagnosis
  • Tremor / genetics

Substances

  • FMR1 protein, human
  • Fragile X Mental Retardation Protein

Supplementary concepts

  • Fragile X Tremor Ataxia Syndrome