One-step production of bioactive proteins through simultaneous PEGylation and refolding

Bioconjug Chem. 2014 Jan 15;25(1):63-71. doi: 10.1021/bc400314f. Epub 2013 Dec 24.

Abstract

Production of protein therapeutics often involves in vitro refolding from bacterial inclusion bodies and subsequent PEGylation to improve protein stability and plasma half-life. Here, we devised a novel strategy for one-step production of site-specific mono-PEGylated proteins with good bioactivity and improved biostability by integrating PEGylation and protein refolding (IPPR). Using lysozyme and recombinant human fibroblast growth factor 21 (rhFGF21) as model proteins, we showed that both PEGylation and refolding of denatured proteins have been simultaneously accomplished by IPPR with high efficiency of refolding yield and bioconjugation. PEGylated rhFGF21 by IPPR has a similar capacity as the native rhFGF21 to stimulate glucose uptake in 3T3-L1 cells, but exhibits prolonged blood glucose and triglyceride lowering activity levels in the ob/ob diabetic mouse model. Hence, IPPR will significantly facilitate the generation of protein therapeutics.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • 3T3-L1 Cells
  • Animals
  • Cells, Cultured
  • Disease Models, Animal
  • Fibroblast Growth Factors / chemistry*
  • Fibroblast Growth Factors / metabolism
  • Humans
  • Mice
  • Mice, Obese
  • Muramidase / chemistry*
  • Muramidase / metabolism
  • Polyethylene Glycols / chemistry*
  • Polyethylene Glycols / metabolism
  • Polyethylene Glycols / pharmacokinetics
  • Protein Refolding*
  • Recombinant Proteins / chemistry
  • Recombinant Proteins / metabolism

Substances

  • Recombinant Proteins
  • fibroblast growth factor 21
  • Polyethylene Glycols
  • Fibroblast Growth Factors
  • Muramidase