A novel nonsense mutation in the EpCAM gene in a patient with congenital tufting enteropathy

J Pediatr Gastroenterol Nutr. 2014 Jan;58(1):18-21. doi: 10.1097/MPG.0000000000000106.

Abstract

Objectives: Tufting enteropathy (TE) is a classical congenital disorder of the intestinal mucosa causing protracted diarrhea in infancy as a result of a dysfunctional epithelial cell barrier, which is mainly caused by mutations in the EpCAM gene and expression of a nonfunctional epithelial cell adhesion molecule in the intestine. We report here a novel nonsense mutation in a patient suspected of having TE, resulting in a complete absence of EpCAM in duodenal enterocytes.

Methods: A patient presenting with congenital diarrhea and suspected of having TE was screened for EpCAM mutations, and duodenal biopsies were stained for EpCAM using immunohistochemistry analysis.

Results: We identified a novel homozygous nonsense mutation in the EpCAM gene in a patient suspected of having TE, causing a complete loss of EpCAM expression in duodenal enterocytes.

Conclusions: With screening analysis for EpCAM mutations and immunohistochemistry for EpCAM expression in duodenal enterocytes, we found a novel homozygous mutation in a patient with classical protracted diarrhea in infancy finally diagnosed as TE, which results in a complete absence of EpCAM and in dysfunctional barrier formation in duodenal enterocytes.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Antigens, Neoplasm / genetics*
  • Antigens, Neoplasm / metabolism
  • Cell Adhesion Molecules / genetics*
  • Cell Adhesion Molecules / metabolism
  • Codon, Nonsense*
  • Diarrhea, Infantile / genetics*
  • Diarrhea, Infantile / metabolism
  • Diarrhea, Infantile / pathology
  • Duodenum / metabolism
  • Duodenum / pathology*
  • Epithelial Cell Adhesion Molecule
  • Female
  • Homozygote*
  • Humans
  • Infant
  • Intestinal Diseases / congenital
  • Intestinal Diseases / genetics*
  • Intestinal Diseases / metabolism
  • Intestinal Diseases / pathology
  • Intestinal Mucosa / metabolism
  • Intestinal Mucosa / pathology*
  • Malabsorption Syndromes / genetics*
  • Malabsorption Syndromes / metabolism
  • Malabsorption Syndromes / pathology

Substances

  • Antigens, Neoplasm
  • Cell Adhesion Molecules
  • Codon, Nonsense
  • EPCAM protein, human
  • Epithelial Cell Adhesion Molecule

Supplementary concepts

  • Diarrhea 5, With Tufting Enteropathy, Congenital