Mutations of DEPDC5 cause autosomal dominant focal epilepsies

Nat Genet. 2013 May;45(5):552-5. doi: 10.1038/ng.2601. Epub 2013 Mar 31.

Abstract

The main familial focal epilepsies are autosomal dominant nocturnal frontal lobe epilepsy, familial temporal lobe epilepsy and familial focal epilepsy with variable foci. A frameshift mutation in the DEPDC5 gene (encoding DEP domain-containing protein 5) was identified in a family with focal epilepsy with variable foci by linkage analysis and exome sequencing. Subsequent pyrosequencing of DEPDC5 in a cohort of 15 additional families with focal epilepsies identified 4 nonsense mutations and 1 missense mutation. Our findings provided evidence of frequent (37%) loss-of-function mutations in DEPDC5 associated with a broad spectrum of focal epilepsies. The implication of a DEP (Dishevelled, Egl-10 and Pleckstrin) domain-containing protein that may be involved in membrane trafficking and/or G protein signaling opens new avenues for research.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Amino Acid Sequence
  • Brain / metabolism
  • Brain / pathology*
  • Case-Control Studies
  • Child
  • Cohort Studies
  • Computational Biology
  • Epilepsies, Partial / diagnosis
  • Epilepsies, Partial / genetics*
  • Exome / genetics*
  • Female
  • Genetic Linkage
  • Genetic Predisposition to Disease / genetics*
  • Genome, Human
  • Genotype
  • Guanine Nucleotide Exchange Factors / genetics*
  • Humans
  • Male
  • Middle Aged
  • Molecular Sequence Data
  • Mutation / genetics*
  • Pedigree
  • Sequence Homology, Amino Acid
  • Young Adult

Substances

  • Guanine Nucleotide Exchange Factors