Restoration of normal L-type Ca2+ channel function during Timothy syndrome by ablation of an anchoring protein

Circ Res. 2011 Jul 22;109(3):255-61. doi: 10.1161/CIRCRESAHA.111.248252. Epub 2011 Jun 23.

Abstract

Rationale: L-type Ca(2+) (Ca(V)1.2) channels shape the cardiac action potential waveform and are essential for excitation-contraction coupling in heart. A gain-of-function G406R mutation in a cytoplasmic loop of Ca(V)1.2 channels causes long QT syndrome 8 (LQT8), a disease also known as Timothy syndrome. However, the mechanisms by which this mutation enhances Ca(V)1.2-LQT8 currents and generates lethal arrhythmias are unclear.

Objective: To test the hypothesis that the anchoring protein AKAP150 modulates Ca(V)1.2-LQT8 channel gating in ventricular myocytes.

Methods and results: Using a combination of molecular, imaging, and electrophysiological approaches, we discovered that Ca(V)1.2-LQT8 channels are abnormally coupled to AKAP150. A pathophysiological consequence of forming this aberrant ion channel-anchoring protein complex is enhanced Ca(V)1.2-LQT8 currents. This occurs through a mechanism whereby the anchoring protein functions like a subunit of Ca(V)1.2-LQT8 channels that stabilizes the open conformation and augments the probability of coordinated openings of these channels. Ablation of AKAP150 restores normal gating in Ca(V)1.2-LQT8 channels and protects the heart from arrhythmias.

Conclusion: We propose that AKAP150-dependent changes in Ca(V)1.2-LQT8 channel gating may constitute a novel general mechanism for Ca(V)1.2-driven arrhythmias.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • A Kinase Anchor Proteins / chemistry
  • A Kinase Anchor Proteins / genetics*
  • A Kinase Anchor Proteins / metabolism
  • Action Potentials / physiology
  • Age Factors
  • Animals
  • Arrhythmias, Cardiac / genetics
  • Arrhythmias, Cardiac / metabolism
  • Arrhythmias, Cardiac / physiopathology
  • Autistic Disorder
  • Calcium / metabolism
  • Calcium Channels, L-Type / chemistry
  • Calcium Channels, L-Type / genetics*
  • Calcium Channels, L-Type / metabolism
  • Cardiomegaly / genetics
  • Cardiomegaly / metabolism
  • Cardiomegaly / physiopathology
  • Ion Channel Gating / physiology
  • Long QT Syndrome / genetics*
  • Long QT Syndrome / metabolism
  • Long QT Syndrome / physiopathology*
  • Mice
  • Mice, Transgenic
  • Myocardial Contraction / physiology
  • Myocytes, Cardiac / physiology*
  • Protein Interaction Domains and Motifs / physiology
  • Syndactyly / genetics*
  • Syndactyly / metabolism
  • Syndactyly / physiopathology*

Substances

  • A Kinase Anchor Proteins
  • Akap5 protein, mouse
  • CACNA1C protein, mouse
  • Calcium Channels, L-Type
  • Calcium

Supplementary concepts

  • Timothy syndrome