Modern approaches to treating acute promyelocytic leukemia

J Clin Oncol. 2011 Feb 10;29(5):495-503. doi: 10.1200/JCO.2010.32.1067. Epub 2011 Jan 10.

Abstract

The advent of all-trans-retinoic acid (ATRA) and its combination with anthracycline-containing chemotherapy have contributed in the past 2 decades to optimize the antileukemic efficacy in acute promyelocytic leukemia (APL), leading to complete remission rates greater than 90%, virtual absence of resistance, and cure rates of nearly 80%. Recently reported studies from large cooperative trials have also shown that more rational delivery of treatment and improved outcomes may derive from the use of risk-adapted protocols. In particular, patients at higher risk of relapse (ie, those presenting with WBC > 10 × 10(9)/L) seem to benefit from treatments that include cytarabine in the ATRA-plus-chemotherapy scheme, whereas patients with standard-risk disease can be successfully managed with less-intensive regimens that contain ATRA and anthracycline-based chemotherapy. After the outstanding results with arsenic trioxide (ATO) in the treatment of APL relapse, several experimental trials have been designed to explore the role of ATO in front-line therapy with the aim not only of minimizing the use of chemotherapy but also to reinforce standard ATRA-plus-chemotherapy regimens and additionally improve therapeutic efficacy. In this review article, we discuss most recent advances in the treatment of patients with newly diagnosed and relapsed APL.

Publication types

  • Review

MeSH terms

  • Antineoplastic Combined Chemotherapy Protocols / therapeutic use
  • Arsenic Trioxide
  • Arsenicals / therapeutic use
  • Brain Neoplasms / therapy
  • Cytarabine / therapeutic use
  • Hematopoietic Stem Cell Transplantation
  • Humans
  • Leukemia, Promyelocytic, Acute / therapy*
  • Oxides / therapeutic use
  • Recurrence
  • Reverse Transcriptase Polymerase Chain Reaction
  • Tretinoin / administration & dosage

Substances

  • Arsenicals
  • Oxides
  • Cytarabine
  • Tretinoin
  • Arsenic Trioxide