Patient Registries and Trial Readiness in Myotonic Dystrophy--TREAT-NMD/Marigold International Workshop Report

Neuromuscul Disord. 2009 Dec;19(12):860-6. doi: 10.1016/j.nmd.2009.08.009. Epub 2009 Oct 20.

Authors

Rachel Thompson¹, Benedikt Schoser, Darren G Monckton, Karla Blonsky, Hanns Lochmüller

Affiliation

¹ TREAT-NMD, Institute of Human Genetics, Newcastle University, Newcastle upon Tyne, NE1 3BZ, UK.

PMID: 19846307
DOI: 10.1016/j.nmd.2009.08.009

No abstract available

Publication types

Congress

MeSH terms

Clinical Trials as Topic*
Databases as Topic
Humans
International Cooperation
Myotonic Dystrophy* / diagnosis
Myotonic Dystrophy* / genetics
Myotonic Dystrophy* / therapy
Registries*
Severity of Illness Index
Treatment Outcome